WVU Medicine Health Report - SMA Gene Replacement Therapy

Monday, February 8, 2021

One in 11,000 babies is born with spinal muscular atrophy or SMA. It's the leading genetic cause of death for infants. But a new gene therapy treatment is saving lives and improving outcomes. In this WVU Medicine Health Report, Sara McGuire, MD, pediatric neurologist, discusses “SMA Gene Replacement Therapy.”